Orphan Drugs Pakistan - Kaunse Rare Disease Medicines Available Nahin?

Orphan Drugs Pakistan - Kaunse Rare Disease Medicines Available Nahin?

Pakistan mein kai aisi rare diseases hain jinke ilaaj ke liye jo medicines chahiye hoti hain, unhe hum “Orphan Drugs” kehte hain. Ye wo dawaiyaan hoti hain jo bahut kam logon ko chahiye hoti hain, is liye pharmaceutical companies inhe commercial level par banane ya import karne mein interest nahi leti. Is article mein hum dekhenge ke Pakistan mein orphan drugs ka kya status hai, kaunse medicines available nahi hain, aur agar kisi patient ko chahiye ho to unhe import karne ke legal tareeqe kya hain.

❓ Orphan Drugs Kya Hoti Hain?

“Orphan drug” ka matlab hai aisi medicine jo rare disease ke treatment ke liye banayi gayi ho. Rare diseases un bimariyon ko kehte hain jinke patients poori population ka ek chhota sa hissa hotay hain. Jaise Europe mein agar 10,000 logon mein 5 ya us se kam log kisi disease se suffer kar rahe hon, to usay rare disease kaha jata hai.

Pharmaceutical companies in medicines par research kam karti hain, kyunki unka commercial profit kam hota hai. Isi wajah se inhe “orphan” yaani “be-sahara” drugs kaha jata hai.

Pakistan Mein Orphan Drugs Ki Situation

Pakistan mein ab tak orphan drug regulation properly define nahi hua. Drug Regulatory Authority of Pakistan (DRAP) ne kuch guidelines issue ki hain, lekin abhi tak koi specific “orphan drug policy” nahi bani. Is wajah se kai medicines import karne mein mushkil hoti hai, aur kuch patients ko black market ya foreign pharmacies ka sahara lena padta hai.

2024 ke data ke mutabiq Pakistan mein 50 se zyada essential life-saving drugs market se gaib thi jinme kuch orphan drugs bhi shamil hain jaise Hydrocortisone, Fludrocortisone, Tegral aur Streptokinase injections.

Common Orphan Drugs Jinki Availability Mushkil Hai

Drug Name	Use / Indication	Availability in Pakistan
Fludrocortisone (Florinef)	Adrenal insufficiency, CAH	Limited / Imported only
Hydrocortisone Injection (Solu-Cortef)	Emergency adrenal crisis in children	Often unavailable
Venetoclax	Chronic Lymphocytic Leukemia	Imported, high-cost
Glasdegib	Acute Myeloid Leukemia (AML)	Rare import only
Tegral (Carbamazepine)	Epilepsy, seizures	Shortage reported

Orphan Drugs Import Kaise Karein?

Agar koi medicine Pakistan mein available nahi hai, to patient ya unke relative legally import kar sakte hain. Iske liye kuch zaroori steps follow karne padte hain:

1. Doctor se prescription letter hasil karein (mention medicine name, strength, dose, duration).
2. DRAP ko application submit karein ya authorized importer se contact karein.
3. Medicine sirf registered international pharmacies se mangwayen (jaise UK, UAE, Turkey).
4. Customs ke through aane wali shipment par hamesha invoice & prescription attach karein.

Pakistan Mein Orphan Drug Access Ke Challenges

• Import cost bohot zyada hoti hai (1 course 2 lakh tak ja sakta hai).
• Temperature-sensitive drugs ke liye cold chain maintain karna mushkil hota hai.
• DRAP ke approval process me delay hota hai.
• Fake ya substandard medicines ka risk bhi rehta hai.

Government aur NGOs Ka Role

Kuch NGOs jaise Pink Pakistan Trust aur Children’s Hospital Lahore aise rare disease patients ki help karti hain jinko orphan drugs chahiye hoti hain. Government ne ab orphan drug policy banane par kaam start kiya hai, jisse future mein patients ko in medicines tak aasani se access mil sake.

⁉️Orphan Drug Policy Pakistan Mein Kyu Zaroori Hai?

Orphan drugs par ek clear policy banne se:

• Patients ko timely ilaaj mil sakega.
• Smuggling aur black market khatam hogi.
• Research aur local manufacturing ko badhawa milega.

🌍 Global Comparison

Europe aur USA me orphan drug policies active hain. Wahan pharmaceutical companies ko tax benefits milte hain agar wo rare disease drugs banayein. Pakistan me abhi yeh incentive system missing hai.

🔬 Research & Development

Pakistan me universities aur pharmaceutical research centers orphan drugs pe kaam start kar rahe hain, lekin funding aur awareness kam hai. Muzammal Pharmacy ke expert kehte hain ke agar government aur private labs collaborate karein to local production possible hai.

Conclusion

Orphan drugs Pakistan mein abhi tak “neglected area” hain. Jab tak government aur pharmaceutical companies milkar ek sustainable supply chain nahi banati, tab tak rare disease patients ko struggle karna padega. Lekin awareness badh rahi hai — aur tum jaise healthcare bloggers is cause ko aage badha rahe ho.

FAQs Orphan Drugs Pakistan

Q1: Orphan drug kya hoti hai?

Ans: Ye wo dawai hoti hai jo kisi rare disease ke liye banayi gayi ho aur commercial level par easily available na ho.

Q2: Pakistan mein orphan drugs kaise mil sakti hain?

Ans: Doctor prescription ke sath authorized importer ya foreign pharmacy se mangwayi ja sakti hain.

Q3: Kya orphan drug lena legal hai?

Ans: Haan, agar DRAP approval aur prescription ho to import legal hai.

Q4: Kaunse orphan drugs Pakistan mein unavailable hain?

Ans: Fludrocortisone, Hydrocortisone injection, Venetoclax, aur Glasdegib jaise drugs limited supply mein hain.

Q5: Kya orphan drugs ki koi list DRAP ne publish ki hai?

Ans: Abhi tak koi official list nahi, lekin government ne draft policy announce ki hai.